In this scholarly study, autologous keratinocytes were transduced with GMP quality gamma-RV containing full-length cDNA series into patient-derived RDEB keratinocytes and fibroblasts ((addition to autologous fibroblasts for intradermal injection (ClinicalTrials

In this scholarly study, autologous keratinocytes were transduced with GMP quality gamma-RV containing full-length cDNA series into patient-derived RDEB keratinocytes and fibroblasts ((addition to autologous fibroblasts for intradermal injection (ClinicalTrials.gov identifier: “type”:”clinical-trial”,”attrs”:”text”:”NCT02493816″,”term_id”:”NCT02493816″NCT02493816), among others are creating a SIN-RV vector containing